Rare Disease Research:

Most patients with severe and life-threatening rare diseases live with
no effective treatment options and no hope.
Clinical trials investigate potential new therapies that may offer hope to
people who haven’t yet found a therapy that works or that they can
tolerate.

Enter your email if you would like Alexion to contact you about a clinical trial:

Our Goal.

Alexion Pharmaceuticals, Inc. is committed to research in rare diseases, and investigating
potential new treatments that have the possibility of transforming patients' lives.