Number of patients meeting the definition of improvement (DOI) at week 24: at least 3 of 6 Core Set Measures (CSM) improved by ≥ 20% with no more than 2 CSM worsening by ≥ 25% (not including the manual muscle testing).

Incidence of treatment-emergent adverse events.

Number of patients improving in Physician and Patient/Parent global activity measurement from baseline

(and 9 more...)

10

All

7 Years and older (Child, Adult, Senior)

NCT02594735

IRB 111418

AID

November 2015

December 2017

December 2017

November 3, 2015

October 27, 2017

2300 M Street, 9th floor. Medical Faculty Associates, The George Washington University.Washington, D.C., District of Columbia, United States