New Therapy Offers Gene Fix for ‘Bubble Boy’ Disease

April 21, 2016

(STAT News) – But if he were born today, Vetter would likely have been the perfect candidate for a new gene therapy technique that seems to get the immune systems of SCID patients back on track. And while previous genetic treatments had been performed on infants, this new approach works in teenagers and young adults, according to a small but promising study published Wednesday.

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