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A report on drug development in neuromuscular diseases as of January 2009

posted on January 1, 2009 - 2:37pm

In the era of molecular biology, the drug development process has moved from a “let’s try it and see what happens” approach to a scientifically based process of discovery and application.
For many of the diseases in MDA’s program, drug discovery begins with gene discovery — identifying a gene that, when flawed, causes a disease.