Most people with Sanfilippo syndrome live into their teenage years. Some patients live longer, while others with severe forms die at an earlier age.

Doctors say symptoms appear most severe with type A Sanfilippo syndrome, the one young Eliza is trying to beat.

Until now the disease has been incurable. However, a new treatment has the O'Neills fighting to raise more than $2 million to have little Eliza enter a gene therapy trial that starts later this year.

If successful, the therapy could save Eliza and stop Sanfilippo Syndrome from destroying her body.

The video of Eliza's story has grabbed the attention of more than 500 people on{}gofundme.com{}and has raised more than $45,000. Eliza's parents hope to raise $1 million through the GoFundMe{}fundraiser in time to save their daughter.{}

All donations will go to support the gene therapy trial at Nationwide Children's Hospital in Columbus, Ohio.

However, the total amount the O'Neills need over the next several months is $2.5 Million.