BioMarin is the world leader in delivering therapeutics that provide meaningful advances to patients who live with serious and life-threatening rare genetic diseases. We target diseases that lack effective therapies and affect relatively small numbers of patients, many of whom are children. These conditions are often inherited, difficult to diagnose, progressively debilitating and have few, if any, treatment options. BioMarin will continue to focus on advancing therapies that are the first or best of their kind. BioMarins Research & Development group is responsible for everything from research and discovery to post-market clinical development. Research & Development involves all bench and clinical research and the associated groups that support those endeavors. Our teams work on developing first-in-class and best-in-class therapeutics that provide meaningful advances to patients who live with rare diseases. Come join our team and make a meaningful impact on patients lives. BioMarin's Novel Vectors Deliver on Gene Therapy's PromiseBioMarin's Vector Biology group is responsible for initiating and guiding gene therapy projects through the research, pre-clinical and clinical phases. This team is lead by Dr. Barrie Carter, the scientist who first introduced using the adeno-associated virus as a gene therapy delivery vehicle. Click here to read more about BioMarin's ground-breaking science in Human Factor VIII Expression and Normalization of Bleeding Following AAV Gene Therapy in a Double Knockout Mouse Model of Hemophilia Click here to read more about BioMarin's plans to progress it's Investigational Gene Therapy for Hemophilia A, into Phase 3 Studies RESPONSIBILITIES: This is a position for a highly innovative, passionate, and energetic Scientist to develop adeno-associated viral vector technologies in an industry setting. The candidate should be extremely motivated to drive drug development.The Principal or Senior Scientist is part of a multidisciplinary research team responsible for using BioMarins Proprietary technology platform to develop gene therapy applications. Responsibilities include:

Experience and ability to work collaboratively in cross-functional teams

Drug development and/or extensive research training EDUCATION:

A Ph.D. in the Biomedical Sciences.

Strong consideration given to Molecular Biologists IMPORTANT NOTE: This role directly handles and/or is in proximity to lentiviral or other viral vector based gene delivery systemsWe are an equal opportunity employer and all qualified applicants will receive consideration for employment without regard to race, color, religion, sex, national origin, disability status, protected veteran status, or any other characteristic protected by law.