intravenous injection

A research team reports 'unprecedented' improvement in newborn SMA-affected mice that received gene therapy via intravenous injection

posted on March 1, 2010 - 6:33pm

Scientists at four U.S. institutions have successfully used gene therapy to treat very young mice with a disease resembling severe spinal muscular atrophy (SMA). Study results were published online Feb. 28, 2010, in the journal Nature Biotechnology.