Fellowship will advance therapeutic strategies for Alpha-1 Antitrypsin DeficiencyCiting “substantial progress” in the first year of a postdoctoral fellowship at the National Institutes of Health’s (NIH) National Center for Advancing Translational Sci...

- RNAi Therapeutic ARC-AAT Induces Dose Dependent Reductions in Mutant AAT Protein of Greater than 95 Percent in Preclinical Studies- Long Duration of Effect with AAT Remaining Reduced by More than 80% at 6 Weeks after a Single Dose- Company ...