The ferocious rally in Vertex Pharmaceuticals shares on results in early stage data for its new cystic fibrosis treatment will surely tempt some investors to exit. That may not be wise, though, as the rally is likely to continue.

The randomized controlled trial has long been held up as the gold standard for testing new drugs. But the nation’s top drug evaluator, Janet Woodcock, believes they aren’t necessary for all new experimental treatments. Randomized trials are long, expensive to run, and ultimately produce limited answers, she said at a medical conference last week. The […]